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FDA approves Rocket's gene therapy Kresladi for rare immune disorder
Rocket Pharmaceuticals has received accelerated FDA approval for Kresladi (marnetegragene autotemcel), its first hematopoietic stem cell-based gene therapy, to treat children with severe leukocyte adhesion deficiency-1 (LAD-1).
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- BioPharma Divebiopharmadive.com
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